Register
Upcoming Conference
Arizona, May 26, 2022



  • Conferences
    • 2022 Arizona State of Reform Health Policy Conference
    • 2022 Inland Northwest State of Reform Health Policy Conference
    • All Conferences
  • Conversations
    • Past Conversations
  • News
    • alaska
    • arizona
    • california
    • colorado
    • florida
    • hawaii
    • maryland
    • michigan
    • oregon
    • texas
    • utah
    • washington
    • Federal
  • Intelligence
    • 5 Things We’re Watching
    • 5 Slides We’re Discussing
    • What They’re Watching
    • Interviews
    • Podcasts
  • Videos
  • ABOUT
  • SUBSCRIBE
  • Conferences
    • 2022 Arizona State of Reform Health Policy Conference
    • 2022 Inland Northwest State of Reform Health Policy Conference
    • All Conferences
  • Conversations
    • Past Conversations
  • News
    • alaska
    • arizona
    • california
    • colorado
    • florida
    • hawaii
    • maryland
    • michigan
    • oregon
    • texas
    • utah
    • washington
    • Federal
  • Intelligence
    • 5 Things We’re Watching
    • 5 Slides We’re Discussing
    • What They’re Watching
    • Interviews
    • Podcasts
  • Videos
  • ABOUT
  • SUBSCRIBE

5 Slides: Gene therapy and the promise for rare disease

November 16, 2021 | Virtual

Overview
Registration

Overview

Gene therapy has yielded promising results for treating various life-threatening rare diseases like muscular dystrophy and cystic fibrosis. This is groundbreaking for individuals living with rare disease, whose limited treatment options often entail ongoing, high-cost medical visits. However, these new treatments are entering the market at considerably high prices and posing affordability challenges for patients. We’ve convened a group of rare disease experts to talk through the potential that gene therapy has to treat rare diseases, and how to navigate their financial barriers.

Date: Tuesday, Nov. 16th, 2021

Time: 12:00 – 1:00pm PT

Panelists:

    • Jennifer Hodge, PhD: US Rare Neurology Medical Team Lead, Pfizer
    • Ryan Fischer: Chief Advocacy Officer, Parent Project Muscular Dystrophy
    • Angela Ramirez Holmes: Founder, Cal Rare

 

Jennifer Hodge is the US Rare Neurology Medical Team Lead at Pfizer. Over the past 9 years, she has contributed in roles of increasing responsibility across Early Pipeline/Gene Therapy, Sickle Cell Disease, Hemophilia and I&I where she played an important role in the US & EU launches of XELJANZ for Rheumatoid arthritis. She received her PhD in Immunology and completed two Post-Doctoral Fellowships at Harvard Medical School & the Yale University School of Medicine.

Ryan Fischer serves as the Chief Advocacy Officer for Parent Project Muscular Dystrophy and has been with the organization for 16 years. Within PPMD, Ryan oversees patient advocacy, patient-focused drug development initiatives including patient-preference research, and the strategic development of the largest patient reported registry in Duchenne developed by PPMD, The Duchenne Registry.

Angela Ramirez Holmes started her advocacy in rare diseases when her 8 year old son was diagnosed with a rare brain condition, an arteriovenous malformation. Angela is the Founder and President of California Action Link for Rare Diseases (Cal Rare), a non-profit membership coalition of rare disease stakeholders that began in 2017 and is dedicated to improving the lives of rare disease patients in California.

Registration

This event is free to attend but registration is required. If you have trouble registering, please send us an email and we will get you taken care of!

Subscribe

Get the latest state-specific policy intelligence for the health care sector delivered to your inbox.

Top 5 Stories in the West Coast Edition

  • Washington State pipe distribution program aims to curb disease and death among drug users
  • Alaska House, Senate pass series of health-related bills
  • Proposed initiative would facilitate psilocybin use in Washington
  • Corrective measures underway at Oregon State Hospitals following April escape of patient
  • Assembly Health Committee advances bill to establish DHCS and Kaiser Permanente direct contract
  • Conferences
    • 2022 Arizona State of Reform Health Policy Conference
    • 2022 Inland Northwest State of Reform Health Policy Conference
    • All Conferences
  • Conversations
    • Past Conversations
  • News
    • alaska
    • arizona
    • california
    • colorado
    • florida
    • hawaii
    • maryland
    • michigan
    • oregon
    • texas
    • utah
    • washington
    • Federal
  • Intelligence
    • 5 Things We’re Watching
    • 5 Slides We’re Discussing
    • What They’re Watching
    • Interviews
    • Podcasts
  • Videos
Tweets by StateofReform
  • 
  • 
  • 
  • 
© 2022 State of Reform. All rights reserved.
Privacy Policy
 

Loading Comments...